How to Use Duchenne muscular dystrophy in a Sentence

Duchenne muscular dystrophy

noun

• Steen died at the age of 25 from Duchenne muscular dystrophy.
  — Elsa Keslassy, Variety, 14 Nov. 2022
• In the 1960s, Dr. Jerry Mendell saw his first patient with Duchenne muscular dystrophy.
  — Jerry Mendell, TIME, 2 May 2024
• And here’s the story of a 5-year-old candidate for a gene therapy for Duchenne muscular dystrophy.
  — Stat Staff, STAT, 28 Dec. 2023
• In the next few weeks, Sarepta Therapeutics will release new data that could change the future of the company and the lives of thousands of patients with Duchenne muscular dystrophy.
  — Jason Mast, STAT, 30 Oct. 2023
• In 2016, parents of children with Duchenne muscular dystrophy pressured the F.D.A. to green-light a drug that had been studied in a single uncontrolled trial of only twelve boys.
  — Gideon Lewis-Kraus, The New Yorker, 19 June 2023
• Jesus and Stacy Zamora’s son, Alex, was diagnosed with Duchenne muscular dystrophy about a decade ago.
  — Caroline Catherman, Orlando Sentinel, 5 July 2022
• The decline is due to unfavorable outcomes from clinical trials for one of its drugs, SRP-9001, used for treating Duchenne muscular dystrophy.
  — Trefis Team, Forbes, 26 Oct. 2021
• Late last year, Pfizer reported the death of a patient in its early-stage trial for a different Duchenne muscular dystrophy gene therapy.
  — Laura Ungar, Fortune, 4 Nov. 2022
• William Jackson -- age two -- has been diagnosed with a rare genetic disease called Duchenne muscular dystrophy.
  — John Canzano, oregonlive, 12 May 2021
• Our colleague Jason Mast joins us to explain how the approval of a landmark gene therapy for Duchenne muscular dystrophy set in motion a frantic race to get children treated before their 6th birthdays.
  — Adam Feuerstein, STAT, 17 Aug. 2023
• The scientist hopes that the research will one day lead to treatments for rare genetic disorders such as Duchenne muscular dystrophy and inherited Alzheimer’s disease.
  — Ed Cara / Gizmodo, Quartz, 2 Apr. 2024
• The agency reached another low the following year, when its leaders overruled their own staff to approve eteplirsen, a treatment for a rare genetic condition called Duchenne muscular dystrophy.
  — Benjamin Mazer, The Atlantic, 13 July 2021
• After his diagnosis of Duchenne muscular dystrophy, a muscle-wasting disease, in June of last year, doctors’ offices became places for needle pokes and anxiety.
  — Marin Wolf, Dallas News, 25 Mar. 2023
• Yet a major benefit is that the gene therapy provides another option for people with Duchenne muscular dystrophy, and it’s administered just once.
  — Jacqueline Howard, CNN, 20 June 2024
• Researchers have found ways to alter or turn off disease-causing genes in leukemia, hemophilia A, spinal muscular atrophy, Duchenne muscular dystrophy, and other diseases.
  — Isabella Cueto, STAT, 10 July 2023
• Sickle cell disease fits into that category, as do cystic fibrosis and Duchenne muscular dystrophy.
  — Katie Hafner, Star Tribune, 30 July 2020
• For genetic conditions like Duchenne muscular dystrophy, there is little doctors can do to slow or treat the condition other than trying to manage symptoms, since only addressing the genetic changes responsible can help halt the disease.
  — Alice Park, Time, 23 June 2023
• The doctors cited an example including Acceleron, a biotechnology company, which used its version of this receptor in clinical trials to treat patients with Duchenne muscular dystrophy.
  — Ashley Strickland, CNN, 7 Sep. 2020
• The company is working on eight preclinical drug programs, with a focus on neuromuscular diseases, including therapies for multiple forms of Duchenne muscular dystrophy, or DMD.
  — Ryan Cross, BostonGlobe.com, 8 Dec. 2022
• These concerns extend to various medical conditions, including ALS, Duchenne muscular dystrophy, cystic fibrosis, and other rare diseases.
  — Jon Hu, STAT, 18 Dec. 2023
• This helps scientists identify the mechanisms behind genetic disorders like Duchenne muscular dystrophy.
  — Molly Glick, Discover Magazine, 26 July 2021

Last Updated: 20 Dec 2024